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PYC-001

Alternative Names: PYC-001, PYC 001, PYC001
Latest Update: 2024-06-14
Latest Update Note: Clinical Trial Update

Product Description

PYC-001 increases expression of the remaining healthy copy of OPA1 to compensate for the protein insufficiency. (Sourced from: https://pyctx.com/disease-areas-adoa/)

Mechanisms of Action: OPA1 Replacer

Novel Mechanism: Yes

Modality: Nucleic Acid

Route of Administration: N/A

FDA Designation: None *

Approval Status: Not Approved

Approved Countries: None

Approved Indications: None

Known Adverse Events: None

Company: PYC Therapeutics
Company Location:
Company CEO:
Additonal Commercial Interests: None

Clinical Description

Map of Global Clinical Trials for PYC-001

Countries in Clinic:

Active Clinical Trial Count: 1

Highest Development Phases

Phase 1: Arthrogryposis|Optic Atrophies, Hereditary|Optic Atrophy, Autosomal Dominant

Trial

Phase

Trial Status

Disease

Primary Completion Date

Probability of Success

Sundew

P1

Not yet recruiting

Optic Atrophies, Hereditary|Arthrogryposis|Optic Atrophy, Autosomal Dominant

2025-07-01

43%

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