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ION-440

Alternative Names: ION-440, ION 440, ION440
Latest Update: 2024-07-24
Latest Update Note: Clinical Trial Update

Product Description

Mechanisms of Action: MECP2 Modulator

Novel Mechanism: Yes

Modality: Nucleic Acid

Route of Administration: Injection

FDA Designation: None *

Approval Status: Not Approved

Approved Countries: None

Approved Indications: None

Known Adverse Events: None

Company: Ionis
Company Location: CARLSBAD CA 92010
Company CEO: Brett P. Monia
Additonal Commercial Interests: None

Clinical Description

Map of Global Clinical Trials for ION-440

Countries in Clinic: Spain

Active Clinical Trial Count: 2

Highest Development Phases

Phase 2: Myelodysplastic Syndrome|Rett Syndrome

Trial

Phase

Trial Status

Disease

Primary Completion Date

Probability of Success

ION440-CS1

P2

Not yet recruiting

Myelodysplastic Syndrome

2030-04-22

ATTUNE

P2

Not yet recruiting

Rett Syndrome

2026-05-01

24%

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