Product Description
SIG-007 is comprised of cells that are genetically modified with a non-viral vector to express human alpha-galactosidase A, or AGAL for the treatment of Fabry disease. (Sourced from: https://ir.sigilon.com/news-releases/news-release-details/sigilon-therapeutics-receives-orphan-drug-designation-sig-007)
Mechanisms of Action: Cell Therapy
Novel Mechanism: No
Modality: Cell Therapy
Route of Administration: Injection
FDA Designation: Orphan Drug - Fabry Disease *
Approval Status: Not Approved
Approved Countries: None
Approved Indications: None
Known Adverse Events: None
Company: Sigilon Therapeutics
Company Location: CAMBRIDGE MA 02142
Company CEO: Rogerio Vivaldi Coelho
Additonal Commercial Interests: None
Clinical Description
Countries in Clinic:
Active Clinical Trial Count:
Highest Development Phases
Phase 0: Fabry Disease
Trial |
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Trial Status |
Disease |
Primary Completion Date |
Probability of Success |
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