Product Description
AT-GTX-701 is a preclinical drug candidate being developed by Amicus for the treatment of Fabry Disease. (Sourced from: https://ir.amicusrx.com/news-releases/news-release-details/amicus-therapeutics-presents-positive-preclinical-fabry-disease)
Mechanisms of Action: Gene Therapy, GLA
Novel Mechanism: No
Modality: Gene Therapy
Route of Administration: Injection
FDA Designation: *
Approval Status: Not Approved
Approved Countries: None
Approved Indications: None
Known Adverse Events: None
Company: Amicus
Company Location: Eastern America
Company Founding Year: 2002
Additional Commercial Interests: None
Clinical Description
Countries in Clinic:
Active Clinical Trial Count:
Recent & Upcoming Milestones
Highest Development Phases
Phase 0: Fabry Disease
Trial ID |
Trial |
Phase |
Trial Status |
Disease |
Primary Completion Date |
Probability of Success |
Latest Trial Update Date |
Data Updated |
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Recent News Events
Date |
Type |
Title |
|---|---|---|
|
02/08/2021 |
News Article |
Amicus Therapeutics Presents Positive Preclinical Fabry Disease Gene Therapy Data at the 17th Annual WORLDSymposium™ 2021 |
