Product Description
Mechanisms of Action: Gene Therapy,CYP4V2
Novel Mechanism: Yes
Modality: Gene Therapy
Route of Administration: Injection
FDA Designation: None *
Approval Status: Not Approved
Approved Countries: None
Approved Indications: None
Known Adverse Events: None
Company: Shanghai Tianze Yuntai Biomedicine Co., Ltd.
Company Location:
Company CEO:
Additional Commercial Interests: None
Clinical Description

Countries in Clinic: China
Active Clinical Trial Count: 3
Highest Development Phases
Phase 3: Corneal Dystrophies, Hereditary|Retinal Dystrophies
Phase 1: Retinal Degeneration
Trial |
Phase |
Trial Status |
Disease |
Primary Completion Date |
Probability of Success |
---|---|---|---|---|---|
VGR-R01-301 | P3 |
Not yet recruiting |
Corneal Dystrophies, Hereditary|Retinal Dystrophies |
2026-12-01 |
|
VGR-R01-101 | P1 |
Not yet recruiting |
Retinal Dystrophies|Corneal Dystrophies, Hereditary |
2025-03-01 |
|
CTR20230237 | P1 |
Not yet recruiting |
Retinal Degeneration |
None |