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BLU-782

Alternative Names: blu-782, blu782, blu 782
Latest Update: 2023-01-11
Latest Update Note: News Article

Product Description

BLU-782 is being developed by Blueprint Medicines for the treatment of patietns with fibrodysplasia ossificans progressiva (FOP). (Sourced from: https://www.blueprintmedicines.com/wp-content/uploads/2019/09/Blueprint-Medicines-ASBMR-2019-BLU-782-Poster1.pdf)

Mechanisms of Action: ALK2 Inhibitor

Novel Mechanism: Yes

Modality: Small Molecule

Route of Administration: Oral

FDA Designation: None *

Approval Status: Not Approved

Approved Countries: None

Approved Indications: None

Known Adverse Events: None

Company: Blueprint Medicines
Company Location: CAMBRIDGE MA 02139
Company CEO: Kathryn Haviland
Additonal Commercial Interests: None

Clinical Description

Countries in Clinic:

Active Clinical Trial Count:

Highest Development Phases

Phase 1: Healthy Volunteers

Trial

Phase

Trial Status

Disease

Primary Completion Date

Probability of Success

BLU-782-0101

P1

Completed

Healthy Volunteers

2019-09-11

28%

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