Product Description
ALN-VSP02 is a RNA interference (RNAi) therapeutic comprised of lipid nanoparticle-formulated small interfering RNAs (siRNAs) targeting the expression of vascular endothelial growth factor (VEGF)-A and kinesin spindle protein (KSP). (Sourced from: https://ascopubs.org/doi/abs/10.1200/jco.2011.29.15_suppl.3025)
Mechanisms of Action: KSP Modulator,VEGF Modulator Binder
Novel Mechanism: Yes
Modality: Nucleic Acid
Route of Administration: Intravenous
FDA Designation: None *
Approval Status: Not Approved
Approved Countries: None
Approved Indications: None
Known Adverse Events: None
Company: Alnylam
Company Location: CAMBRIDGE MA 02142
Company CEO: Yvonne L. Greenstreet
Additional Commercial Interests: None
Clinical Description
Countries in Clinic:
Active Clinical Trial Count:
Highest Development Phases
Phase 1: Oncology Solid Tumor Unspecified|Liver Cancer
Trial |
Phase |
Trial Status |
Disease |
Primary Completion Date |
Probability of Success |
---|---|---|---|---|---|
ALN-VSP02-002 | P1 |
Completed |
Liver Cancer |
2012-08-01 |
|
ALN-VSP02-001 | P1 |
Completed |
Oncology Solid Tumor Unspecified |
2011-07-01 |